evaluatepharma orphan drug report 2014 infographic

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Leader Board: 2020 R&D Spend vs. Return on Investment By 2020: Worldwide orphan drug sales forecast to be $176 billion. Compound Annual Growth Rate for orphan drugs will be 2x overall drug market, excluding generics. BMY Sales Drug R&D Revlimid (lenalidomide) VX-809 + Ivacaftor BMY set to climb to #1 position in orphan drug sales in 2020 #1 orphan drug in 2020 Most valuable R&D orphan drug Phase III orphan drug development costs ½ that of non-orphan drugs, potentially ¼ after US tax breaks. Phase III orphan drugs expected ROI to be 1.89x non-orphan drugs. Median Cost per Patient Differential 19x higher for orphan drugs Compared to non-orphan $98,534 vs $5,153 $755 million | Orphan (Top 10) Avg. USA Sales 5 Years After Launch (2013 FDA Approvals) Avg. Phase III Trial Size (2013 FDA Approvals) $1,755 million | Non-Orphan (Top 10) 1,310 patients | Orphan (Top 10) Orphan Drugs Sales 2020 Non-Orphan Drugs Orphan drugs will be 19.1% of worldwide prescription sales, excluding generics. Trends in Sales Download the full report at www.evaluategroup.com/orphandrug2014 Copyright @ 2014 Evaluate Ltd. All rights reserved. 6,811 patients | Non-Orphan (Top 10) Orphan Drug Report 2014

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Infographic based on EvaluatePharma's Orphan Drug Report 2014 - providing a top-level insight, from the world's financial markets, into the expected performance of the orphan drug market between now and 2020. Full report available to download free at www.evaluategroup.com/orphandrug2014

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Page 1: EvaluatePharma Orphan Drug Report 2014 Infographic

Leader Board: 2020

R&D Spend vs. Return on Investment

By 2020:Worldwide orphan drug sales forecast

to be $176 billion.

Compound Annual Growth Rate

for orphan drugs will be 2x overall drug market,excluding generics.

BMYSales

Drug

R&D

Revlimid (lenalidomide)

VX-809 + Ivacaftor

BMY set to climb to #1 position in orphan drug sales in 2020

#1 orphan drug in 2020

Most valuable R&D orphan drug

Phase III orphan drug development

costs ½ that of non-orphan drugs,

potentially ¼ after US tax breaks.

Phase III orphan drugs expected ROI

to be 1.89x non-orphan drugs.

Median Cost per Patient Differential

19x higher for orphan drugs

Compared to non-orphan

$98,534 vs $5,153

$755 million | Orphan (Top 10)

Avg. USA Sales 5 Years After Launch(2013 FDA Approvals)

Avg. Phase III Trial Size(2013 FDA Approvals)

$1,755 million | Non-Orphan (Top 10)

1,310 patients | Orphan (Top 10)

Orphan Drugs

Sales 2020

Non-Orphan Drugs

Orphan drugs will be 19.1% of worldwide prescription sales, excluding generics.

Trends in Sales

Download the full report at www.evaluategroup.com/orphandrug2014Copyright @ 2014 Evaluate Ltd. All rights reserved.

6,811 patients | Non-Orphan (Top 10)

Orphan Drug Report 2014